Ignite Creation Date:
2025-12-18 @ 8:12 AM
Ignite Modification Date:
2025-12-18 @ 8:12 AM
Study NCT ID:
NCT06488924
Status:
None
Last Update Posted:
2025-09-02 00:00:00
First Post:
2024-06-28 00:00:00
Is Possible Gene Therapy:
False
Has Adverse Events:
False
Brief Title:
An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB
Sponsor:
None
Organization:
Study Overview
Official Title:
An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB
Status:
None
Status Verified Date:
2025-08
Last Known Status:
None
Delayed Posting:
No
If Stopped, Why?:
Not Stopped
Has Expanded Access:
False
If Expanded Access, NCT#:
N/A
Has Expanded Access, NCT# Status:
N/A
Acronym:
None
Brief Summary:
A Phase I/ II, open-label study, designed to evaluate the safety and explore efficacy of the study drug in development for the treatment of MPS IIIB patients.
Detailed Description:
None
Study Oversight
Has Oversight DMC:
None
Is a FDA Regulated Drug?:
None
Is a FDA Regulated Device?:
None
Is an Unapproved Device?:
None
Is a PPSD?:
None
Is a US Export?:
None
Is an FDA AA801 Violation?: