Ignite Creation Date:
2024-10-26 @ 3:42 PM
Last Modification Date:
2024-10-26 @ 3:42 PM
Study NCT ID:
NCT06627543
Status:
ENROLLING_BY_INVITATION
Last Update Posted:
None
First Post:
2024-09-29
Brief Title:
Effect of Enzyme Replacement Therapy on Cardiac Function in Children With Gaucher Disease Type 3
Sponsor:
None
Organization:
None
Study Overview
Official Title:
Effect of Enzyme Replacement Therapy on Cardiac Function in Children With Gaucher Disease Type 3
Status:
ENROLLING_BY_INVITATION
Status Verified Date:
2024-10
Last Known Status:
None
Delayed Posting:
No
If Stopped, Why?:
Not Stopped
Has Expanded Access:
No
If Expanded Access, NCT#:
N/A
Has Expanded Access, NCT# Status:
N/A
Acronym:
None
Brief Summary:
all cases confirmed diagnosis of Gaucher disease type 3 recieving enzyme replacement therapy at Assiut university hospital
Detailed Description:
evaluate cardiac involvement in a group of GD type 3 patients evaluate pulmonary hypertension and valvular involvement compare the findings of basic echo before the start of replacement therapy as well as with healthy controls to assess the effects of enzyme replacement therpay on the cardiac function
Study Oversight
Has Oversight DMC:
None
Is a FDA Regulated Drug?:
None
Is a FDA Regulated Device?:
None
Is an Unapproved Device?:
None
Is a PPSD?:
None
Is a US Export?:
None
Is an FDA AA801 Violation?:
None