Viewing StudyNCT00215527



Ignite Creation Date: 2024-05-05 @ 12:02 PM
Last Modification Date: 2024-10-26 @ 9:18 AM
Study NCT ID: NCT00215527
Status: TERMINATED
Last Update Posted: 2013-02-21
First Post: 2005-09-19

Brief Title: Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis MPS I
Sponsor: Patricia I Dickson MD
Organization: Dickson Patricia I MD

Conditions & Keywords Data

Conditions:
Name
Spinal Cord Compression
Mucopolysaccharidosis I
Lysosomal Storage Diseases
Keywords:
Name View
LA Biomed View
mucopolysaccharidosis View
Hurler-Scheie View
Scheie View
laronidase View
spinal cord compression View
central nervous system View
enzyme replacement therapy View
intrathecal View