Viewing StudyNCT00004454



Ignite Creation Date: 2024-05-05 @ 11:07 AM
Last Modification Date: 2024-10-26 @ 9:04 AM
Study NCT ID: NCT00004454
Status: COMPLETED
Last Update Posted: 2005-06-24
First Post: 1999-10-18

Brief Title: Phase III Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II Mild Hunter Syndrome
Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development NICHD
Organization: Office of Rare Diseases ORD

Conditions & Keywords Data

Conditions:
Name
Mucopolysaccharidosis II
Keywords:
Name View
rare disease View
inborn errors of metabolism View
mucopolysaccharidosis View
mucopolysaccharidosis II View