Ignite Creation Date:
2024-05-06 @ 3:33 PM
Last Modification Date:
2024-10-26 @ 1:51 PM
Study NCT ID:
NCT04669535
Status:
ACTIVE_NOT_RECRUITING
Last Update Posted:
2023-12-14
First Post:
2020-11-23
Brief Title:
A Dose-escalation and Safety Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease
Sponsor:
Terence Flotte
Organization:
University of Massachusetts Worcester