Viewing StudyNCT00004378



Ignite Creation Date: 2024-05-05 @ 11:20 AM
Last Modification Date: 2024-10-26 @ 9:04 AM
Study NCT ID: NCT00004378
Status: COMPLETED
Last Update Posted: 2005-06-24
First Post: 1999-10-18

Brief Title: Stem Cell Transplantation SCT for Genetic Diseases
Sponsor: National Center for Research Resources NCRR
Organization: National Center for Research Resources NCRR

Conditions & Keywords Data

Conditions:
Name
Inborn Errors of Metabolism
Thrombocytopenia
Metachromatic Leukodystrophy
Fanconis Anemia
Thalassemia Major
Pure Red-Cell Aplasia
Keywords:
Name View
thalassemia major View
Fanconis anemia View
amegakaryocytic thrombocytopenia View
aplastic anemia View
congenital pure red cell aplasia View
genetic diseases and dysmorphic syndromes View
hematologic disorders View
inborn errors of metabolism View
metachromatic leukodystrophy View
pure red cell aplasia View
rare disease View
sphingolipidoses View