Viewing StudyNCT06255782



Ignite Creation Date: 2024-05-06 @ 8:06 PM
Last Modification Date: 2024-10-26 @ 3:20 PM
Study NCT ID: NCT06255782
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-06-28
First Post: 2023-12-19

Brief Title: An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency OTC-HOPE
Sponsor: iECURE Inc
Organization: iECURE Inc

Conditions & Keywords Data

Conditions:
Name
Urea Cycle Disorders Inborn
Ornithine Transcarbamylase Deficiency
Ornithine Transcarbamylase Deficiency Disease
Ornithine Carbamoyltransferase Deficiency Disorder
Keywords:
Name View
Amino Acid Metabolism Inborn Errors View
Ammonia View
Brain Diseases View
Brain Diseases Metabolic View
Brain Diseases Metabolic Inborn View
Central Nervous System Diseases View
Genetic Diseases Inborn View
Genetic Diseases X-Linked View
High Ammonia View
Hyperammonemia View
Inborn View
Inborn Errors View
Liver Disease View
Liver Transplant View
Metabolism View
Metabolic Diseases View
Metabolism Inborn Errors View
Neonatal View
Nervous System Diseases View
NH4 View
Ornithine View
Ornithine Transcarbamylase Deficiency View
OTC View
OTC Deficiency View
OTCD View
Transcarbamylase View
UCD View
Urea Cycle Disorders View
X-Linked View