Viewing Study NCT04105166


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Ignite Modification Date: 2025-12-24 @ 4:44 PM
Study NCT ID: NCT04105166
Status: COMPLETED
Last Update Posted: 2025-09-05
First Post: 2019-09-24
Is Possible Gene Therapy: True
Has Adverse Events: False

Brief Title: Gene Therapy for Pyruvate Kinase Deficiency (PKD)
Sponsor: Rocket Pharmaceuticals Inc.
Organization:

Key Dates - Follows AllAPIJSON File Order

Start Date: 2020-07-06
Start Date Type: ACTUAL
Primary Completion Date: 2025-06-09
Primary Completion Date Type: ACTUAL
Completion Date: 2025-06-09
Completion Date Type: ACTUAL
First Submit Date: 2019-09-24
First Submit QC Date: None
Study First Post Date: 2019-09-26
Study First Post Date Type: ACTUAL
Results First Submit Date: None
Results First Submit QC Date: None
Results First Post Date: None
Results First Post Date Type: None
Results First Post QC Date: None
Results First Post QC Date Type: None
Disp First Submit Date: None
Disp First Submit QC Date: None
Disp First Post Date: None
Disp First Post Date Type: None
Last Update Submit Date: 2025-08-29
Last Update Post Date: 2025-09-05
Last Update Post Date Type: ESTIMATED