Viewing StudyNCT04669535



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Last Modification Date: 2024-10-26 @ 1:51 PM
Study NCT ID: NCT04669535
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2023-12-14
First Post: 2020-11-23

Brief Title: A Dose-escalation and Safety Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease
Sponsor: Terence Flotte
Organization: University of Massachusetts Worcester

Key Dates - Follows AllAPIJSON File Order

Start Date: 2021-01-15
Start Date Type: ACTUAL
Primary Completion Date: 2024-11
Primary Completion Date Type: ESTIMATED
Completion Date: 2028-06
Completion Date Type: ESTIMATED
First Submit Date: 2020-11-23
First Submit QC Date: December 8 2020
Study First Post Date: 2020-12-17
Study First Post Date Type: ACTUAL
Results First Submit Date: None
Results First Submit QC Date: None
Results First Post Date: None
Results First Post Date Type: None
Results First Post QC Date: None
Results First Post QC Date Type: None
Disp First Submit Date: None
Disp First Submit QC Date: None
Disp First Post Date: None
Disp First Post Date Type: None
Last Update Submit Date: 2023-12-13
Last Update Post Date: 2023-12-14
Last Update Post Date Type: ACTUAL