Ignite Creation Date:
2025-12-25 @ 12:52 AM
Ignite Modification Date:
2025-12-25 @ 12:52 AM
Study NCT ID:
NCT02193867
Status:
TERMINATED
Last Update Posted:
2019-11-18
First Post:
2014-07-07
Is Possible Gene Therapy:
False
Has Adverse Events:
True
Brief Title:
Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency