Viewing Study NCT07221760


Ignite Creation Date: 2025-12-25 @ 2:12 AM
Ignite Modification Date: 2026-01-18 @ 6:53 PM
Study NCT ID: NCT07221760
Status: NOT_YET_RECRUITING
Last Update Posted: 2025-10-28
First Post: 2025-10-24
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Personalized Antisense Oligonucleotide for A Single Participant (nL62541) With ATN1 Gene Mutation
Sponsor: n-Lorem Foundation
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module