Viewing Study NCT01721733

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Study NCT ID: NCT01721733

Status: COMPLETED

Last Update Posted: 2020-08-31

First Post: 2012-11-01

Is NOT Gene Therapy: True

Has Adverse Events: False

Brief Title: Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome

Sponsor: PTC Therapeutics

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module