Viewing Study NCT03687333


Ignite Creation Date: 2025-12-25 @ 3:01 AM
Ignite Modification Date: 2026-01-08 @ 2:09 AM
Study NCT ID: NCT03687333
Status: COMPLETED
Last Update Posted: 2022-04-13
First Post: 2018-09-24
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Evaluate Efficacy and Safety in Chinese Patients With Infantile-Onset Pompe Disease With One Year Alglucosidase Alfa Treatment
Sponsor: Genzyme, a Sanofi Company
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module