Viewing Study NCT05175105


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Study NCT ID: NCT05175105
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-11-28
First Post: 2021-11-22
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Not Regularly Transfused, Followed by a 5-Year Extension Period
Sponsor: Agios Pharmaceuticals, Inc.
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module