Viewing Study NCT07014020

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Ignite Creation Date: 2025-12-25 @ 4:17 AM

Ignite Modification Date: 2026-01-12 @ 1:52 PM

Study NCT ID: NCT07014020

Status: RECRUITING

Last Update Posted: 2025-07-30

First Post: 2025-05-21

Is NOT Gene Therapy: True

Has Adverse Events: False

Brief Title: RB001 Gene Therapy Study in Children With SHANK3-related Phelan McDermid Syndrome (PMS)

Sponsor: Peking University First Hospital

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module