Viewing Study NCT02047461

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Ignite Modification Date: 2025-12-27 @ 9:08 PM

Study NCT ID: NCT02047461

Status: COMPLETED

Last Update Posted: 2023-10-17

First Post: 2014-01-09

Is Gene Therapy: True

Has Adverse Events: True

Brief Title: Safety & Efficacy Study of ORGN001 (Formerly ALXN1101) in Pediatric Patients With MoCD Type A Currently Treated With rcPMP

Sponsor: Origin Biosciences

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module Adverse Events Module Baseline Characteristics Module Participant Flow Module