Viewing Study NCT07125066

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Ignite Creation Date: 2025-12-24 @ 4:13 PM

Ignite Modification Date: 2026-01-04 @ 11:14 PM

Study NCT ID: NCT07125066

Status: ENROLLING_BY_INVITATION

Last Update Posted: 2025-08-15

First Post: 2025-07-30

Is NOT Gene Therapy: True

Has Adverse Events: False

Brief Title: An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA)

Sponsor: Jerry Vockley, MD, PhD

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module