Viewing Study NCT03950050


Ignite Creation Date: 2025-12-24 @ 5:20 PM
Ignite Modification Date: 2025-12-24 @ 5:20 PM
Study NCT ID: NCT03950050
Status: COMPLETED
Last Update Posted: 2023-02-14
First Post: 2018-08-06
Is Possible Gene Therapy: False
Has Adverse Events: False

Brief Title: Ambroxol Therapy for Patients With Type 1 Gaucher Disease and Suboptimal Response to Enzyme Replacement Therapy
Sponsor: Shaare Zedek Medical Center
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module