Viewing Study NCT05747261

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Ignite Creation Date: 2025-12-24 @ 11:45 AM

Ignite Modification Date: 2026-01-14 @ 4:52 AM

Study NCT ID: NCT05747261

Status: RECRUITING

Last Update Posted: 2024-02-22

First Post: 2023-02-14

Is NOT Gene Therapy: True

Has Adverse Events: False

Brief Title: Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene After a Single Intravenous Administration of Escalating Doses in Children With Spinal Muscular Atrophy (BLUEBELL)

Sponsor: Biocad

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module