Viewing Study NCT04174157


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Study NCT ID: NCT04174157
Status: RECRUITING
Last Update Posted: 2025-01-31
First Post: 2019-09-12
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
Sponsor: Novartis Pharmaceuticals
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module