Viewing Study NCT04798235


Ignite Creation Date: 2025-12-24 @ 10:30 PM
Ignite Modification Date: 2025-12-25 @ 8:03 PM
Study NCT ID: NCT04798235
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2023-05-09
First Post: 2021-02-22
Is Possible Gene Therapy: True
Is NOT Gene Therapy: False
Has Adverse Events: False

Brief Title: First-in-Human Study of TSHA-101 Gene Therapy for Treatment of Infantile Onset GM2 Gangliosidosis
Sponsor: Dr. Anupam Sehgal
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module