Viewing Study NCT04273269

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Ignite Creation Date: 2025-12-24 @ 11:04 PM

Ignite Modification Date: 2025-12-25 @ 8:35 PM

Study NCT ID: NCT04273269

Status: TERMINATED

Last Update Posted: 2023-06-09

First Post: 2020-01-21

Is Possible Gene Therapy: True

Is NOT Gene Therapy: False

Has Adverse Events: False

Brief Title: A Safety and Efficacy Study of LYS-GM101 Gene Therapy in Patients With GM1 Gangliosidosis

Sponsor: LYSOGENE

Organization:

Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module