Viewing Study NCT02618512


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Study NCT ID: NCT02618512
Status: TERMINATED
Last Update Posted: 2018-04-17
First Post: 2015-10-21
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 Administered Intravenously
Sponsor: Alexion Pharmaceuticals, Inc.
Organization: