Viewing Study NCT05523206


Ignite Creation Date: 2025-12-26 @ 5:20 PM
Ignite Modification Date: 2026-01-22 @ 8:34 AM
Study NCT ID: NCT05523206
Status: COMPLETED
Last Update Posted: 2025-01-30
First Post: 2022-08-29
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: A Natural History Study of Biomarkers and Clinical Outcomes in Mucopolysaccharidosis Type IIIA (MPS IIIA; Sanfilippo Syndrome)
Sponsor: Sanguine Biosciences
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module