Viewing Study NCT04480567


Ignite Creation Date: 2025-12-25 @ 12:29 AM
Ignite Modification Date: 2026-01-07 @ 7:53 PM
Study NCT ID: NCT04480567
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-12-12
First Post: 2020-07-08
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: AAV Gene Therapy Study for Subjects with PKU
Sponsor: BioMarin Pharmaceutical
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module