Viewing Study NCT04120493


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Ignite Modification Date: 2026-01-05 @ 5:21 PM
Study NCT ID: NCT04120493
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-10-21
First Post: 2019-09-30
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Safety and Proof-of-Concept (POC) Study With AMT-130 in Adults With Early Manifest Huntington's Disease
Sponsor: UniQure Biopharma B.V.
Organization:

Study Modules

Identification Module Status Module Sponsor Collaborators Module Oversight Module Description Module Conditions Module Design Module Arms Interventions Module Outcomes Module Eligibility Module Contacts Locations Module References Module