Viewing StudyNCT04669535



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Last Modification Date: 2024-10-26 @ 1:51 PM
Study NCT ID: NCT04669535
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2023-12-14
First Post: 2020-11-23

Brief Title: A Dose-escalation and Safety Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease
Sponsor: Terence Flotte
Organization: University of Massachusetts Worcester

Organization Data

Organization: University of Massachusetts Worcester
Class: OTHER
Study ID: AXO-GM2-001
Study Type: None
Study Domain: None
Study Link: None
Lead Sponsor: Terence Flotte
Lead Sponsor Class: OTHER
Responsible Party: Terence Flotte
Responsible Party Title: Dean
Responsible Party Type: SPONSOR_INVESTIGATOR
Responsible Party Affiliation: University of Massachusetts Worcester
Old Name: None
Old Organization: None

Collaborators

Name Class
University of Massachusetts Worcester OTHER
Massachusetts General Hospital OTHER