Viewing StudyNCT04669535



Ignite Creation Date: 2024-05-06 @ 3:33 PM
Last Modification Date: 2024-10-26 @ 1:51 PM
Study NCT ID: NCT04669535
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2023-12-14
First Post: 2020-11-23

Brief Title: A Dose-escalation and Safety Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease
Sponsor:
Organization: University of Massachusetts Worcester