Ignite Creation Date:
2025-12-24 @ 8:03 PM
Ignite Modification Date:
2026-06-28 @ 8:30 PM
Study NCT ID:
NCT02171104
Status:
RECRUITING
Last Update Posted:
2025-08-03
First Post:
2014-06-20
Is NOT Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
Sponsor:
Masonic Cancer Center, University of Minnesota
Organization:
Conditions & Keywords Data
Conditions:
Conditions
| Condition Brief | Condition Text | View |
|---|---|---|
| None | Mucopolysaccharidosis Disorders | View |
| None | Hurler Syndrome | View |
| None | Hunter Syndrome | View |
| None | Maroteaux Lamy Syndrome | View |
| None | Sly Syndrome | View |
| None | Alpha-Mannosidosis | View |
| None | Fucosidosis | View |
| None | Aspartylglucosaminuria | View |
| None | Glycoprotein Metabolic Disorders | View |
| None | Sphingolipidoses | View |
| None | Recessive Leukodystrophies | View |
| None | Globoid Cell Leukodystrophy | View |
| None | Metachromatic Leukodystrophy | View |
| None | Niemann-Pick B | View |
| None | Niemann-Pick C Subtype 2 | View |
| None | Sphingomyelin Deficiency | View |
| None | Peroxisomal Disorders | View |
| None | Adrenoleukodystrophy With Cerebral Involvement | View |
| None | Zellweger Syndrome | View |
| None | Neonatal Adrenoleukodystrophy | View |
| None | Infantile Refsum Disease | View |
| None | Acyl-CoA Oxidase Deficiency | View |
| None | D-Bifunctional Enzyme Deficiency | View |
| None | Multifunctional Enzyme Deficiency | View |
| None | Alpha-methylacyl-CoA Racmase Deficiency | View |
| None | Mitochondrial Neurogastrointestingal Encephalopathy | View |
| None | Severe Osteopetrosis | View |
| None | Hereditary Leukoencephalopathy With Axonal Spheroids (HDLS; CSF1R Mutation) | View |
| None | Inherited Metabolic Disorders | View |